Recent Advancements Across Rare Inherited Neuromuscular Disorders

USD 250.00

* Required Fields

USD 250.00


Be the first to review this product

This edition of the Genetic Technology TOE depicts life sciences trends across rare inherited neuromuscular disorders. Innovative business and societal strategies involving comprehensive value assessment, stakeholders’ engagement, novel reimbursement approaches, and new manufacturing approaches for producing orphan drugs are critical to bypass many of the present technological, regulatory, and financial challenges. The corresponding clinical trials scenario for lysosomal storage disorders is also presented in the TOE.The Genetic Technology TechVision Opportunity Engine (TOE) presents the latest R&D developments and advances with an emphasis on opportunities to profit in the explosive field of genetic technolo

Table of Contents

Recent Advancements Across Rare Inherited Neuromuscular DisordersEnhancing Therapeutics Associated with Rare Inherited Neuromuscular Disorders Site-directed Enzyme Enhancement Therapy for Inherited DiseasesRecombinant Enzyme Therapy for Lysosomal Storage DisordersComputational Biology and Machine Learning for Orphan DiseasesAdeno Associated Virus Gene Therapy for Neuromuscular Diseases Clinical Trials and Industry InteractionsInterventional Studies Industry Interactions

Why Frost & Sullivan

Working with the CEO’s growth team to create a vision based on a transformation growth strategy

Creating content-based digital marketing strategies that leverage our research perspective to differentiate and “tell your story”

Tracking over 1000 emerging technologies and analyzing the impact by industry and application to reveal the companies to watch in each sector

The Frost & Sullivan team is based in our 45 global offices and have developed a powerful global understandings of how industries operate on a global level.